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RNA therapies are here - Ready or not

Thursdays, 12.00 noon - 1.30 pm. Royal Newcastle Centre Lecture Theatre

Lunch
12.00 noon - 12.30 pm, RNC Boardroom (3125)

Presentation
12.30 pm – 1.30 pm, RNC Lecture Theatre or join us online via Zoom

Other years  2023  


02 May 2024 by Immunology

Dr Theo de Malmanche - Director, Immunology

UpToDate logo Cardiac amyloidosis: Epidemiology, clinical manifestations, and diagnosis

Open Access logo Ding F, Wickman L, Wang SQ, Zhang Y, Wang F, Afshinnia F, Hodgin J, Ding J, Wiggins RC. Accelerated podocyte detachment and progressive podocyte loss from glomeruli with age in Alport Syndrome. Kidney Int. 2017 Dec;92(6):1515-1525. doi: 10.1016/j.kint.2017.05.017. Epub 2017 Jul 26. PMID: 28754557; PMCID: PMC5696060.

Open Access logo Gomez IG, MacKenna DA, Johnson BG, Kaimal V, Roach AM, Ren S, Nakagawa N, Xin C, Newitt R, Pandya S, Xia TH, Liu X, Borza DB, Grafals M, Shankland SJ, Himmelfarb J, Portilla D, Liu S, Chau BN, Duffield JS. Anti-microRNA-21 oligonucleotides prevent Alport nephropathy progression by stimulating metabolic pathways. J Clin Invest. 2015 Jan;125(1):141-56. doi: 10.1172/JCI75852. Epub 2014 Nov 21. PMID: 25415439; PMCID: PMC4382246.

Open Access logo Smith ES, Whitty E, Yoo B, Moore A, Sempere LF, Medarova Z. Clinical Applications of Short Non-Coding RNA-Based Therapies in the Era of Precision Medicine. Cancers (Basel). 2022 Mar 21;14(6):1588. doi: 10.3390/cancers14061588. PMID: 35326738; PMCID: PMC8946086.

Open Access logo Mohamed M, Abu Lila AS, Shimizu T, Alaaeldin E, Hussein A, Sarhan HA, Szebeni J, Ishida T. PEGylated liposomes: immunological responses. Sci Technol Adv Mater. 2019 Jun 26;20(1):710-724. doi: 10.1080/14686996.2019.1627174. PMID: 31275462; PMCID: PMC6598536.

Open Access logo Adams D, Gonzalez-Duarte A, O'Riordan WD, Yang CC, Ueda M, Kristen AV, et al. Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis. N Engl J Med. 2018 Jul 5;379(1):11-21. PubMed PMID: 29972753. eng.

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